Starting the conversation on gene therapy for phenylketonuria: Current perspectives of patients, caregivers, and advocates
- Regier, D.S.
- Bąk, A.
- Bausell, H.
- O'Reilly, E.
- Cowsert, L.M.
Journal:
Molecular Genetics and Metabolism Reports
ISSN: 2214-4269
Year of publication: 2022
Volume: 31
Type: Article